3-methylglutaconic aciduria type 3

MeSH: C535311ORPHA: 67047

Overview

3-methylglutaconic aciduria that has material basis in mutation in the OPA3 gene

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with 3-methylglutaconic aciduria type 3, sourced from HPO and Orphanet clinical annotations.

Visual impairmentNystagmusIntellectual disabilityAtaxiaDysarthriaChoreoathetosisGait disturbanceSpastic paraparesis3-Methylglutaconic aciduria

Classification & Codes

MeSH Code

C535311

Orphanet Code

ORPHA:67047
3-methylglutaconic aciduria type 3
MeSHC535311
OrphanetORPHA:67047
Treatments0 drug(s)
Symptoms on record9 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO