3-methylglutaconic aciduria type 5

MeSH: C565706ORPHA: 66634

Overview

3-methylglutaconic aciduria that has material basis in homozygous mutation in the DNAJC19 gene on chromosome 3q26

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with 3-methylglutaconic aciduria type 5, sourced from HPO and Orphanet clinical annotations.

AtaxiaGrowth delayDilated cardiomyopathyElevated circulating glutaric acid concentration3-Methylglutaconic aciduriaIntrauterine growth retardationProlonged QT intervalIncreased circulating lactate concentrationDelayed gross motor developmentElevated circulating hepatic transaminase concentrationHypochromic microcytic anemiaNormochromic microcytic anemiaNeurodevelopmental delayPerineal hypospadiasOptic atrophySeizureMicrovesicular hepatic steatosisNeonatal hypoglycemiaBilateral cryptorchidismHypoplasia of penisMuscular ventricular septal defectHypothyroidismNeonatal hypotoniaMuscle weaknessDystoniaAbnormal facial shapeLower limb spasticityAction tremorDevelopmental regressionGeneralized amyotrophyBilateral basal ganglia lesionsAtrophy/Degeneration affecting the brainstemBilateral sensorineural hearing impairmentRepetitive compulsive behaviorDiaphragmatic eventrationDyskinesiaArachnoid cyst

Classification & Codes

MeSH Code

C565706

Orphanet Code

ORPHA:66634
3-methylglutaconic aciduria type 5
MeSHC565706
OrphanetORPHA:66634
Treatments0 drug(s)
Symptoms on record37 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO