46,XY disorder of sex development due to isolated 17,20-lyase deficiency

ORPHA: 90796

Overview

human disease

Available Treatments (0)

No treatments linked yet

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Clinical Presentation

Signs and symptoms associated with 46,XY disorder of sex development due to isolated 17,20-lyase deficiency, sourced from HPO and Orphanet clinical annotations.

Hypoplasia of the uterusHypospadiasMicropenisDecreased fertilityPolycystic ovariesPrimary amenorrheaHypergonadotropic hypogonadismDelayed pubertyOsteoporosisSparse axillary hairSparse pubic hairSparse body hairDelayed skeletal maturationReduced bone mineral densityAbsence of secondary sex characteristicsPrimary gonadal insufficiencyDecreased serum estradiolElevated circulating follicle stimulating hormone levelEnlarged polycystic ovariesElevated circulating luteinizing hormone levelAbnormal circulating corticosterone levelDecreased circulating androgen concentrationDecreased serum testosterone concentrationDysmenorrheaCryptorchidismDecreased fertility in femalesShort statureHypoplasia of the vaginaDecreased testicular sizeDecreased fertility in malesAmbiguous genitalia, maleMale pseudohermaphroditismGynecomastiaFailure to thriveFemale external genitalia in individual with 46,XY karyotypeAbnormal sex determination

Classification & Codes

Orphanet Code

ORPHA:90796
46,XY disorder of sex development due to isolated 17,20-lyase deficiency
OrphanetORPHA:90796
Treatments0 drug(s)
Symptoms on record36 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
46,XY disorder of sex development due to isolated 17,20-lyase deficiency | OrphanDrug