acetazolamide-responsive myotonia

ORPHA: 99736

Overview

Acetazolamide-responsive myotonia is a form of potassium-aggravated myotonia (PAM, see this term) which shows dramatic improvement with the use of acetazolamide (ACZ)

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with acetazolamide-responsive myotonia, sourced from HPO and Orphanet clinical annotations.

OphthalmoparesisOphthalmoplegiaHypothyroidismHypertoniaGait disturbanceDysphagiaMyotoniaMyalgiaMuscle spasmEMG abnormalitySkeletal muscle hypertrophyChest pain

Classification & Codes

Orphanet Code

ORPHA:99736
acetazolamide-responsive myotonia
OrphanetORPHA:99736
Treatments0 drug(s)
Symptoms on record12 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO