acyl-CoA dehydrogenase 9 deficiency

MeSH: C567006ORPHA: 99901

Overview

Acyl-CoA dehydrogenase 9 (ACAD9) deficiency is a rare disorder leading to a deficiency of complex I of the respiratory chain and is characterized by neurological dysfunction, hepatic failure and cardiomyopathy

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with acyl-CoA dehydrogenase 9 deficiency, sourced from HPO and Orphanet clinical annotations.

Decreased activity of mitochondrial complex IGeneralized hypotoniaEncephalopathyHepatic steatosisFailure to thriveCongestive heart failureHypertrophic cardiomyopathyDilated cardiomyopathyThrombocytopeniaHyperammonemiaIncreased circulating lactate concentrationElevated circulating hepatic transaminase concentrationLactic acidosisMyopathyDecreased circulating carnitine concentrationGeneralized muscle weaknessMyalgiaEMG: myopathic abnormalitiesFatigable weaknessProlonged prothrombin timeElevated creatine kinase after exerciseIncreased circulating lactate dehydrogenase concentrationElevated circulating acylcarnitine concentrationSudden cardiac deathNonketotic hypoglycemiaCerebral edemaDicarboxylic aciduriaAcute hepatic failureCerebellar hemorrhage

Classification & Codes

MeSH Code

C567006

Orphanet Code

ORPHA:99901
acyl-CoA dehydrogenase 9 deficiency
MeSHC567006
OrphanetORPHA:99901
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
acyl-CoA dehydrogenase 9 deficiency | OrphanDrug