adrenomyodystrophy

MeSH: C538051ORPHA: 977

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with adrenomyodystrophy, sourced from HPO and Orphanet clinical annotations.

MegacystisAbnormality of the urinary systemMegalocorneaSeizureHypotoniaHepatic steatosisFailure to thriveAbnormal intestine morphologyDelayed skeletal maturationMyopathyEMG abnormalityShort statureReduced bone mineral densityGeneralized hyperpigmentationPrimary adrenal insufficiencySevere global developmental delay

Classification & Codes

MeSH Code

C538051

Orphanet Code

ORPHA:977
adrenomyodystrophy
MeSHC538051
OrphanetORPHA:977
Treatments0 drug(s)
Symptoms on record16 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO