adult-onset basal ganglia disease

MeSH: C548080ORPHA: 157846

Overview

Neuroferritinopathy is a late-onset type of neurodegeneration with brain iron accumulation (NBIA; see this term) characterized by progressive chorea or dystonia and subtle cognitive deficits

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with adult-onset basal ganglia disease, sourced from HPO and Orphanet clinical annotations.

DystoniaAbnormal basal ganglia morphologyDecreased circulating ferritin concentrationIron accumulation in brainCognitive impairmentHypomimic faceEmotional labilityDysarthriaGait disturbanceDysphoniaDysphagiaBradykinesiaChoreaOrofacial dyskinesiaAbnormal caudate nucleus morphologyEye of the tiger anomaly of globus pallidusInvoluntary movementsFocal dystoniaIron accumulation in substantia nigraT2 hypointense thalamusAbnormal thalamic MRI signal intensityLeg dystoniaAbnormal putamen morphologyAbnormal dentate nucleus morphologyBlepharospasmParkinsonismBrisk reflexesWeak voiceLoss of voiceCaudate atrophyWriter's crampLower limb hyperreflexiaUpper limb hyperreflexiaImpaired smooth pursuitPalatal tremorArm dystoniaPsychosisFrontal lobe dementiaResting tremorIncreased CSF protein concentrationBabinski signSubcortical dementiaUpgaze palsy

Classification & Codes

MeSH Code

C548080

Orphanet Code

ORPHA:157846
adult-onset basal ganglia disease
MeSHC548080
OrphanetORPHA:157846
Treatments0 drug(s)
Symptoms on record43 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
adult-onset basal ganglia disease | OrphanDrug