AICA-ribosiduria

MeSH: C563876ORPHA: 250977

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with AICA-ribosiduria, sourced from HPO and Orphanet clinical annotations.

Fused labia minoraWide mouthThin upper lip vermilionBrachycephalyLow-set earsSeizureCongenital blindnessClitoral hypertrophySevere intellectual disabilityProminent forehead

Classification & Codes

MeSH Code

C563876

Orphanet Code

ORPHA:250977
AICA-ribosiduria
MeSHC563876
OrphanetORPHA:250977
Treatments0 drug(s)
Symptoms on record10 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO