Alpers' disease

ORPHA: 726

Overview

cerebral degeneration that results in progressive degeneration of grey matter in the cerebrum and has symptom convulsions

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Alpers' disease, sourced from HPO and Orphanet clinical annotations.

MicrocephalyAbnormality of the eyeAbnormality of visionBlindnessAtaxiaHypotoniaSpasticityComaGlobal developmental delayChoreoathetosisAreflexiaMyoclonusBilateral tonic-clonic seizureProgressive spasticitySpastic paraparesisDevelopmental regressionParaparesisFocal-onset seizureAbnormality of movement

Classification & Codes

Orphanet Code

ORPHA:726
Alpers' disease
OrphanetORPHA:726
Treatments0 drug(s)
Symptoms on record19 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
Alpers' disease | OrphanDrug