artemis deficiency

ORPHA: 275

Overview

severe combined immunodeficiency characterized by being T cell-negative, B cell-negative and natural killer cell-positive with sensitivity to ionizing radiation and that has material basis in mutation in the DCLRE1C gene on chromosome 10p13

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with artemis deficiency, sourced from HPO and Orphanet clinical annotations.

Decreased total T cell countDecreased total B cell countAutoimmune hemolytic anemiaBronchiectasisRecurrent bacterial infectionsDecreased circulating IgA concentrationDecreased circulating IgG concentrationRecurrent opportunistic infectionsCutaneous abscessVerrucaeRecurrent upper and lower respiratory tract infectionsCutaneous granulomaOtitis mediaSkin rashVitiligoFailure to thriveAutoimmune thrombocytopeniaIntractable diarrheaNeoplasmAutoimmunityRecurrent viral infectionsJuvenile rheumatoid arthritisChronic oral candidiasisRecurrent aphthous stomatitisRecurrent mycobacterial infectionsRecurrent gastroenteritisHashimoto thyroiditis

Classification & Codes

Orphanet Code

ORPHA:275
artemis deficiency
OrphanetORPHA:275
Treatments0 drug(s)
Symptoms on record27 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO