Arts syndrome

MeSH: C535388ORPHA: 1187

Overview

Lethal ataxia with deafness and optic atrophy (also known as Arts syndrome) is characterized by intellectual deficit, early-onset hypotonia, ataxia, delayed motor development, hearing impairment and loss of vision due to optic atrophy

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Arts syndrome, sourced from HPO and Orphanet clinical annotations.

Visual impairmentBlindnessOptic atrophyMuscle weaknessMutismRecurrent infectionsRecurrent upper respiratory tract infectionsDecreased motor nerve conduction velocityEMG: chronic denervation signsSevere demyelination of the white matterAbnormality of somatosensory evoked potentialsCongenital sensorineural hearing impairmentAbnormal erythrocyte enzyme concentration or activitySevere infectionNeck muscle weaknessNystagmusAtaxiaMild intellectual disabilityMotor delayAreflexiaModerate intellectual disabilityTetraplegiaHypouricemiaRespiratory failure requiring assisted ventilationSpinal cord dorsal column hypomyelinationAxial hypotoniaPeripheral neuropathyEEG with focal epileptiform dischargesProfound sensorineural hearing impairmentAppendicular hypotonia

Classification & Codes

MeSH Code

C535388

Orphanet Code

ORPHA:1187
Arts syndrome
MeSHC535388
OrphanetORPHA:1187
Treatments0 drug(s)
Symptoms on record30 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO