ataxia-telangiectasia-like disorder

MeSH: C565779ORPHA: 251347

Overview

autosomal recessive condition caused by mutation(s) in the MRE11A gene, encoding double-strand break repair protein MRE11. It is characterized by progressive cerebellar degeneration resulting in ataxia and oculomotor apraxia

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with ataxia-telangiectasia-like disorder, sourced from HPO and Orphanet clinical annotations.

AtaxiaMask-like faciesSlow saccadic eye movementsOculomotor apraxiaDysarthriaCerebellar atrophyGeneralized hypotoniaDysmetriaReduced tendon reflexesCerebellar vermis hypoplasiaDystoniaGait ataxiaChoreaIntention tremorDilated fourth ventricleOrofacial dyskinesiaAbsent Achilles reflexEnlarged interhemispheric fissureAbnormality of ocular smooth pursuitGaze-evoked nystagmusDysmetric saccadesDelayed speech and language developmentHypergonadotropic hypogonadismMyoclonusJoint hypermobilityPes cavusDysdiadochokinesisDroolingFrequent fallsHyperactive deep tendon reflexesSensorimotor neuropathyVertical nystagmusSmall posterior fossaShort stature

Classification & Codes

MeSH Code

C565779

Orphanet Code

ORPHA:251347
ataxia-telangiectasia-like disorder
MeSHC565779
OrphanetORPHA:251347
Treatments0 drug(s)
Symptoms on record34 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO