atypical pantothenate kinase-associated neurodegeneration

ORPHA: 216873

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with atypical pantothenate kinase-associated neurodegeneration, sourced from HPO and Orphanet clinical annotations.

Emotional labilityDepressionIrritabilitySpasticityDysarthriaParkinsonismHyperreflexiaRigidityLimb dystoniaUpper motor neuron dysfunctionFocal dystoniaViolent behaviorImpulsivityCompulsive behaviorsGait disturbanceTremorDysphagiaChoreaAbnormal speech patternAbnormal pyramidal signOromandibular dystoniaInertiaCognitive impairmentRetinopathyBlindnessOptic atrophyPsychosisClumsinessFrequent fallsTongue atrophy

Classification & Codes

Orphanet Code

ORPHA:216873
atypical pantothenate kinase-associated neurodegeneration
OrphanetORPHA:216873
Treatments0 drug(s)
Symptoms on record30 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO