Autoimmune Pulmonary Alveolar Proteinosis

ICD-10: CA61.0MeSH: D011648ORPHA: 7471 Treatment Available

Overview

A rare lung disorder characterized by accumulation of surfactant proteins in alveoli due to autoantibodies against GM-CSF. Patients experience progressive dyspnea and are at increased risk for opportunistic infections. Global prevalence is estimated at 1 in 100,000.

Available Treatments (1)

DrugFormStatusCountriesLead Time
GM-CSF
Orphan Cold Chain
Powder for solutionFDA Approved1

Clinical Presentation

Signs and symptoms associated with Autoimmune Pulmonary Alveolar Proteinosis, sourced from HPO and Orphanet clinical annotations.

Intraalveolar phospholipid accumulationCyanosisClubbingAbnormality of the upper respiratory tractRestrictive ventilatory defectDyspneaFoam cellsAbnormal circulating protein concentrationHypoxemiaIncreased circulating lactate dehydrogenase concentrationAutoimmune antibody positivityDecreased DLCOCoughCrazy paving patternCracklesWeight lossFeverHemoptysisFatigueChest pain

Classification & Codes

ICD-10 Code

CA61.0

MeSH Code

D011648

Orphanet Code

ORPHA:747
Autoimmune Pulmonary Alveolar Proteinosis
ICD-10CA61.0
MeSHD011648
OrphanetORPHA:747
Treatments1 drug(s)
Symptoms on record20 signs
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/21/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO