autosomal dominant limb-girdle muscular dystrophy type 1F

MeSH: C564242ORPHA: 55595

Overview

autosomal dominant limb-girdle muscular dystrophy that has material basis in heterozygous mutation in the TNPO3 gene on chromosome 7q32

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C564242

Orphanet Code

ORPHA:55595
autosomal dominant limb-girdle muscular dystrophy type 1F
MeSHC564242
OrphanetORPHA:55595
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO