autosomal dominant pure spastic paraplegia

ORPHA: 100980

Overview

Autosomal dominant form of pure hereditary spastic paraplegia

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

Orphanet Code

ORPHA:100980
autosomal dominant pure spastic paraplegia
OrphanetORPHA:100980
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO