autosomal recessive distal spinal muscular atrophy 1
MeSH: C536880ORPHA: 98920
Overview
human disease
Available Treatments (0)
No treatments linked yet
Clinical trials or compassionate use may be available — consult a specialist.
Classification & Codes
MeSH Code
C536880Orphanet Code
ORPHA:98920autosomal recessive distal spinal muscular atrophy 1
| MeSH | C536880 |
| Orphanet | ORPHA:98920 |
| Treatments | 0 drug(s) |
| Status | published |
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO