autosomal recessive distal spinal muscular atrophy 2

MeSH: C535715ORPHA: 139552

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C535715

Orphanet Code

ORPHA:139552
autosomal recessive distal spinal muscular atrophy 2
MeSHC535715
OrphanetORPHA:139552
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO