autosomal recessive limb-girdle muscular dystrophy type 2S

ORPHA: 369840

Overview

autosomal recessive limb-girdle muscular dystrophy that has material basis in homozygous mutation in the TRAPPC11 gene on chromosome 4q35

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with autosomal recessive limb-girdle muscular dystrophy type 2S, sourced from HPO and Orphanet clinical annotations.

CataractHyporeflexiaGait disturbanceAbsent speechHepatomegalyWaddling gaitElevated circulating hepatic transaminase concentrationMyopathyHyperlordosisMyalgiaMuscle spasmMuscular dystrophyProximal muscle weaknessLimb-girdle muscular dystrophyBorderline intellectual disabilityCerebral white matter atrophyAbnormal circulating creatine kinase concentrationMuscle fiber atrophyMicrocephalyHepatic steatosisBilateral tonic-clonic seizureChoreaTruncal ataxiaFloppy infantExophoria

Classification & Codes

Orphanet Code

ORPHA:369840
autosomal recessive limb-girdle muscular dystrophy type 2S
OrphanetORPHA:369840
Treatments0 drug(s)
Symptoms on record25 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO