autosomal semi-dominant severe lipodystrophic laminopathy

ORPHA: 280365

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with autosomal semi-dominant severe lipodystrophic laminopathy, sourced from HPO and Orphanet clinical annotations.

MicrognathiaNarrow nasal ridgeDiabetes mellitusInsulin resistanceXanthomatosisHypertriglyceridemiaPremature graying of hairHepatomegalySkeletal muscle hypertrophyMinimal subcutaneous fatReduced subcutaneous adipose tissueProgeroid facial appearanceAplasia/Hypoplasia of the skinLipodystrophyLipoatrophyPolycystic ovariesIncreased facial adipose tissueRound faceIncreased adipose tissue around the neckSecondary amenorrheaAcanthosis nigricansThin skinHepatic steatosisAbnormal nail morphologyAcroosteolysis of distal phalanges (feet)AtherosclerosisDecreased HDL cholesterol concentrationDecreased serum leptinLoss of subcutaneous adipose tissue in limbsPrecocious atherosclerosisAccelerated atherosclerosisAdvanced eruption of teethMuscle hypertrophy of the lower extremitiesIncreased intraabdominal fatOsteolytic defects of the phalanges of the handDecreased adiponectin levelProximal upper limb muscle hypertrophyCongestive heart failureHypertrophic cardiomyopathyCoronary artery atherosclerosisPancreatitisSplenomegalyGeneralized hirsutismMyopathyMyalgiaSupraventricular arrhythmiaAbnormal atrioventricular conductionDysmenorrheaVentricular arrhythmia

Classification & Codes

Orphanet Code

ORPHA:280365
autosomal semi-dominant severe lipodystrophic laminopathy
OrphanetORPHA:280365
Treatments0 drug(s)
Symptoms on record49 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO