beta-thalassemia-X-linked thrombocytopenia syndrome

MeSH: C564050ORPHA: 231393

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with beta-thalassemia-X-linked thrombocytopenia syndrome, sourced from HPO and Orphanet clinical annotations.

SplenomegalyThrombocytopeniaAbnormal bleedingAnemiaAbnormal platelet functionAbnormal hemoglobin

Classification & Codes

MeSH Code

C564050

Orphanet Code

ORPHA:231393
beta-thalassemia-X-linked thrombocytopenia syndrome
MeSHC564050
OrphanetORPHA:231393
Treatments0 drug(s)
Symptoms on record6 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
beta-thalassemia-X-linked thrombocytopenia syndrome | OrphanDrug