biotin-responsive basal ganglia disease
MeSH: C537658ORPHA: 65284
Overview
Human disease
Available Treatments (0)
No treatments linked yet
Clinical trials or compassionate use may be available — consult a specialist.
Classification & Codes
MeSH Code
C537658Orphanet Code
ORPHA:65284biotin-responsive basal ganglia disease
| MeSH | C537658 |
| Orphanet | ORPHA:65284 |
| Treatments | 0 drug(s) |
| Status | published |
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO