bone dysplasia, lethal Holmgren type

MeSH: C565896ORPHA: 18422 Treatments Available

Available Treatments (2)

DrugFormStatusCountriesLead Time
calcium carbonate
oral tablet 500mg, 600mg, 1000mg; chewable tablet 500mgFDA Approved83d
vitamin D3
oral capsule 1000IU, 2000IU, 5000IU; liquid drops 400IU/dropFDA Approved83d

Clinical Presentation

Signs and symptoms associated with bone dysplasia, lethal Holmgren type, sourced from HPO and Orphanet clinical annotations.

Short ribsNarrow chestWeight lossRespiratory insufficiencySkeletal dysplasiaAbnormal femur morphologyMicromeliaSevere short-limb dwarfismRhizomeliaHigh foreheadHearing abnormalityDepressed nasal ridgeAnteverted naresShort neckAbnormal diaphysis morphologyAbnormal thumb morphologyHypotoniaJoint dislocationBell-shaped thoraxFrontal bossingAbnormal epiphysis morphologyAbnormality of the elbowFlat faceAbnormal cardiovascular system morphologyMetaphyseal dysplasiaAbnormality of the handFailure to thriveAtrial septal defectHypertrophic cardiomyopathyPatent ductus arteriosusTalipesAnemiaDiarrheaNausea and vomitingRecurrent respiratory infectionsHepatomegalyRedundant neck skinHerniaJoint hypermobility

Classification & Codes

MeSH Code

C565896

Orphanet Code

ORPHA:1842
bone dysplasia, lethal Holmgren type
MeSHC565896
OrphanetORPHA:1842
Treatments2 drug(s)
Symptoms on record39 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO