branchiooculofacial syndrome

ORPHA: 1297

Overview

autosomal dominant disease that is characterized by low birth weight and growth retardation, bilateral branchial clefts

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with branchiooculofacial syndrome, sourced from HPO and Orphanet clinical annotations.

Posteriorly rotated earsEverted lower lip vermilionAbnormal pinna morphologyConductive hearing impairmentColobomaAtypical scarring of skinHemangiomaDeep philtrumPostauricular pitPreauricular pitSupraauricular pitHigh palateDolichocephalyWide nasal bridgeBroad nasal tipNasolacrimal duct obstructionUpslanted palpebral fissureIris colobomaMicrodontiaIntrauterine growth retardationHypernasal speechAbnormal speech patternPremature graying of hairShort statureTooth agenesisNon-midline cleft of the upper lipFingernail dysplasiaMulticystic kidney dysplasiaRenal agenesisHydronephrosisOrofacial cleftMicrocorneaStrabismusPtosisCataractPreaxial hand polydactylyUpper lip pit

Classification & Codes

Orphanet Code

ORPHA:1297
branchiooculofacial syndrome
OrphanetORPHA:1297
Treatments0 drug(s)
Symptoms on record37 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO