carnitine-acylcarnitine translocase deficiency

MeSH: C562812ORPHA: 159

Overview

medical condition

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with carnitine-acylcarnitine translocase deficiency, sourced from HPO and Orphanet clinical annotations.

LethargyGlobal developmental delayEncephalopathyMuscle weaknessCardiomyopathyHypoketotic hypoglycemiaHyperammonemiaRespiratory insufficiencyHepatomegalyHypotensionElevated circulating hepatic transaminase concentrationFasting hypoglycemiaRhabdomyolysisDicarboxylic aciduriaDecreased circulating carnitine concentrationVentricular tachycardiaElevated creatine kinase after exerciseArrhythmiaElevated circulating acylcarnitine concentrationIrritabilityMicrocephalyNystagmusCyanosisSeizureComaHepatic failureHypothermiaSudden episodic apneaOliguria

Classification & Codes

MeSH Code

C562812

Orphanet Code

ORPHA:159
carnitine-acylcarnitine translocase deficiency
MeSHC562812
OrphanetORPHA:159
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO