cerebellar ataxia type 43

ORPHA: 497764

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with cerebellar ataxia type 43, sourced from HPO and Orphanet clinical annotations.

Peripheral axonal neuropathyDistal upper limb muscle weaknessDistal lower limb muscle weaknessHypometric saccadesPectus carinatumDysarthriaHyporeflexiaAreflexiaPes cavusGait ataxiaLimb ataxiaUnsteady gaitCogwheel rigidityDistal sensory impairmentDecreased number of large peripheral myelinated nerve fibersDistal amyotrophySensorimotor neuropathyFoot dorsiflexor weaknessPainProgressive cerebellar ataxiaCerebellar vermis atrophy

Classification & Codes

Orphanet Code

ORPHA:497764
cerebellar ataxia type 43
OrphanetORPHA:497764
Treatments0 drug(s)
Symptoms on record21 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO