Charcot-Marie-Tooth disease axonal type 2X

ORPHA: 466775

Overview

Charcot-Marie-Tooth disease type 2 that has material basis in homozygous or compound heterozygous mutation in the SPG11 gene on chromosome 15q21

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

Orphanet Code

ORPHA:466775
Charcot-Marie-Tooth disease axonal type 2X
OrphanetORPHA:466775
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO