Charcot-Marie-Tooth disease type 2B1

MeSH: C537990ORPHA: 98856

Overview

Charcot-Marie-Tooth disease type 2 that has material basis in homozygous mutation in the lamin A/C gene (LMNA) on chromosome 1q22

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Charcot-Marie-Tooth disease type 2B1, sourced from HPO and Orphanet clinical annotations.

Distal sensory impairmentDecreased number of peripheral myelinated nerve fibersSensory axonal neuropathyAxonal lossEMG: axonal abnormalityMotor axonal neuropathyDecreased amplitude of sensory action potentialsDistal lower limb muscle weaknessAxonal degenerationAreflexiaAbnormal foot morphologyPes cavusHammertoeDistal muscle weaknessSteppage gaitDecreased number of large peripheral myelinated nerve fibersDistal amyotrophyProximal muscle weaknessDistal upper limb amyotrophyProximal lower limb amyotrophyDistal upper limb muscle weaknessProximal lower limb muscle weaknessPeroneal muscle atrophyHand muscle atrophyToe extensor amyotrophyHand muscle weaknessInability to walkShoulder girdle muscle atrophyProximal amyotrophyDecreased number of small peripheral myelinated nerve fibersPelvic girdle muscle atrophyDecreased motor nerve conduction velocity

Classification & Codes

MeSH Code

C537990

Orphanet Code

ORPHA:98856
Charcot-Marie-Tooth disease type 2B1
MeSHC537990
OrphanetORPHA:98856
Treatments0 drug(s)
Symptoms on record32 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO