Charcot-Marie-Tooth disease type 2E

MeSH: C537994ORPHA: 99939

Overview

Charcot-Marie-Tooth disease type 2 that has material basis in heterozygous mutation in the light polypeptide neurofilament protein gene (NEFL) on chromosome 8p21

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Charcot-Marie-Tooth disease type 2E, sourced from HPO and Orphanet clinical annotations.

Gait disturbanceAbnormal foot morphologyPeripheral axonal neuropathyUpper limb muscle weaknessSensorimotor neuropathyDemyelinating motor neuropathyLower limb muscle weaknessDemyelinating sensory neuropathyHyporeflexiaPes cavusTalipes calcaneovalgusDistal muscle weaknessEMG: myopathic abnormalitiesSomatic sensory dysfunctionDistal amyotrophyProximal muscle weaknessDifficulty runningAbnormal motor evoked potentialsExtremely elevated creatine kinaseDecreased/absent ankle reflexesMotor delayInability to walkSteppage gaitDecreased nerve conduction velocity

Classification & Codes

MeSH Code

C537994

Orphanet Code

ORPHA:99939
Charcot-Marie-Tooth disease type 2E
MeSHC537994
OrphanetORPHA:99939
Treatments0 drug(s)
Symptoms on record24 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO