Charcot-Marie-Tooth disease type 4B2

MeSH: C535421ORPHA: 99956

Overview

Charcot-Marie-Tooth disease type 4 that has material basis in mutation in the SBF2 gene

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Charcot-Marie-Tooth disease type 4B2, sourced from HPO and Orphanet clinical annotations.

Gait disturbanceAbnormal foot morphologyAreflexia of lower limbsMyelin outfoldingsPoor fine motor coordinationDecreased distal sensory nerve action potentialLower limb muscle weaknessDistal upper limb muscle weaknessDistal lower limb muscle weaknessGlaucomaVocal cord paralysisDysphoniaPes cavusScoliosisKyphoscoliosisDistal sensory impairmentProximal lower limb muscle weaknessAreflexia of upper limbsTongue muscle weaknessSensorineural hearing impairmentPtosisCataractBuphthalmosOptic atrophyAutistic behaviorPenetrating foot ulcersDevelopmental glaucomaMotor delaySpecific learning disabilityTremorPes planusRespiratory insufficiencyInability to walkReduced vital capacityParesthesiaProximal upper limb muscle weaknessTongue atrophyTip-toe gaitHand muscle weaknessWeakness of facial musculature

Classification & Codes

MeSH Code

C535421

Orphanet Code

ORPHA:99956
Charcot-Marie-Tooth disease type 4B2
MeSHC535421
OrphanetORPHA:99956
Treatments0 drug(s)
Symptoms on record40 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO