Charcot-Marie-Tooth disease type 4D

MeSH: C535716ORPHA: 99950

Overview

Charcot-Marie-Tooth disease type 4 that has material basis in homozygous mutation in the N-myc downstream-regulated gene-1 (NDRG1) on chromosome 8q24

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Charcot-Marie-Tooth disease type 4D, sourced from HPO and Orphanet clinical annotations.

Decreased motor nerve conduction velocityDecreased amplitude of sensory action potentialsDemyelinating peripheral neuropathyDistal lower limb muscle weaknessSensorineural hearing impairmentMotor delayAbnormal foot morphologyUnsteady gaitDistal muscle weaknessLower limb amyotrophySplit handPes cavusHammertoePostural tremorInability to walkKyphoscoliosisDistal sensory impairmentSomatic sensory dysfunctionProximal muscle weaknessDistal upper limb muscle weaknessUpper limb amyotrophySkewfoot

Classification & Codes

MeSH Code

C535716

Orphanet Code

ORPHA:99950
Charcot-Marie-Tooth disease type 4D
MeSHC535716
OrphanetORPHA:99950
Treatments0 drug(s)
Symptoms on record22 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO