Charcot-Marie-Tooth disease X-linked recessive 2

MeSH: C535302ORPHA: 101076

Overview

Charcot-Marie-Tooth disease X-linked that has material basis in variation in the region Xp22.2

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Charcot-Marie-Tooth disease X-linked recessive 2, sourced from HPO and Orphanet clinical annotations.

AreflexiaGait disturbancePes cavusHand tremorDistal sensory impairmentSteppage gaitDecreased motor nerve conduction velocityEMG: chronic denervation signsDistal lower limb amyotrophyIntrinsic hand muscle atrophyFoot dorsiflexor weaknessDistal lower limb muscle weaknessTibialis anterior muscle atrophyPeroneal muscle weaknessHand muscle weaknessSensorineural hearing impairmentOptic disc pallorOptic neuropathyIntellectual disabilityHyporeflexiaHyperreflexiaSpastic paraparesisBabinski signHyperactive deep tendon reflexesSlow decrease in visual acuityClasp-knife sign

Classification & Codes

MeSH Code

C535302

Orphanet Code

ORPHA:101076
Charcot-Marie-Tooth disease X-linked recessive 2
MeSHC535302
OrphanetORPHA:101076
Treatments0 drug(s)
Symptoms on record26 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO