Charcot-Marie-Tooth disease X-linked recessive 3

MeSH: C535303ORPHA: 101077

Overview

Charcot-Marie-Tooth disease X-linked that has material basis in variation in the region Xq26

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Charcot-Marie-Tooth disease X-linked recessive 3, sourced from HPO and Orphanet clinical annotations.

Gait disturbanceMotor delayAreflexiaAbnormal foot morphologyPes cavusDecreased motor nerve conduction velocitySomatic sensory dysfunctionDistal amyotrophySensorimotor neuropathyEquinovarus deformityDistal lower limb amyotrophyIntrinsic hand muscle atrophyFoot dorsiflexor weaknessProgressive distal muscle weaknessHand muscle weaknessDelayed ability to walkHyporeflexiaTremorHip dysplasiaRestrictive ventilatory defectInability to walkScoliosisPeripheral axonal neuropathyDemyelinating peripheral neuropathyDistal upper limb amyotrophyPes valgusProximal lower limb muscle weakness

Classification & Codes

MeSH Code

C535303

Orphanet Code

ORPHA:101077
Charcot-Marie-Tooth disease X-linked recessive 3
MeSHC535303
OrphanetORPHA:101077
Treatments0 drug(s)
Symptoms on record27 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO