Cockayne syndrome type 1

ORPHA: 90321

Overview

Cockayne syndrome caused by mutation(s) in the ERCC8 gene, encoding DNA excision repair protein ERCC-8

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Cockayne syndrome type 1, sourced from HPO and Orphanet clinical annotations.

Hearing impairmentDeeply set eyePigmentary retinopathyCutaneous photosensitivityIntellectual disabilityFailure to thriveAbnormal facial shapeBasal ganglia calcificationElevated circulating hepatic transaminase concentrationAbsent brainstem auditory responsesFoot joint contracturePostnatal growth retardationProteinuriaAbnormality of the dentitionLong faceMandibular prognathiaVisual impairmentCataractDecreased lacrimationOptic atrophyHypertensionHypohidrosisAtaxiaGait disturbanceTremorHyperreflexiaDiarrheaPostural instabilityScoliosisAbnormality of peripheral nerve conductionIncreased blood urea nitrogenAbnormality of temperature regulationProgeroid facial appearanceRenal insufficiencyShort chinMacrotiaStrabismusConjunctivitisAnophthalmiaUveitisPhotophobiaNystagmusAnodontiaDelayed eruption of primary teethHypermelanotic maculeSeizureHypotoniaAnemiaLower limb spasticityHepatomegalySleep disturbanceEnamel hypoplasiaWidely spaced primary teethHypoplasia of the primary teethScarringMale hypogonadismCryptorchidism

Classification & Codes

Orphanet Code

ORPHA:90321
Cockayne syndrome type 1
OrphanetORPHA:90321
Treatments0 drug(s)
Symptoms on record57 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO