combined immunodeficiency due to ORAI1 deficiency

MeSH: C557826ORPHA: 317428

Overview

deficiency is a form of CID due to Calcium release activated Ca2+ (CRAC) channel dysfunction (see this term) characterized by recurrent infections, congenital myopathy, ectodermal dysplasia and anhydrosis

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C557826

Orphanet Code

ORPHA:317428
combined immunodeficiency due to ORAI1 deficiency
MeSHC557826
OrphanetORPHA:317428
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO