combined immunodeficiency due to STIM1 deficiency

MeSH: C557827ORPHA: 317430

Overview

deficiency is a form of CID due to Calcium release activated Ca2+(CRAC) channel dysfunction (see this term) characterized by recurrent infections, autoimmunity, congenital myopathy and ectodermal dysplasia

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C557827

Orphanet Code

ORPHA:317430
combined immunodeficiency due to STIM1 deficiency
MeSHC557827
OrphanetORPHA:317430
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO