congenital high-molecular-weight kininogen deficiency

MeSH: C537060ORPHA: 483

Overview

rare autosomal recessive inherited disorder characterized by prolonged partial thromboplastin time and absence of bleeding diathesis

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C537060

Orphanet Code

ORPHA:483
congenital high-molecular-weight kininogen deficiency
MeSHC537060
OrphanetORPHA:483
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO