congenital hyperinsulinism

MeSH: D044903ORPHA: 6571 Treatment Available

Overview

genetic disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
diazoxide
Orphan
Oral suspension, 50mg/mLFDA Approved, EMA Approved614d

Classification & Codes

MeSH Code

D044903

Orphanet Code

ORPHA:657
congenital hyperinsulinism
MeSHD044903
OrphanetORPHA:657
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO