congenital sucrase-isomaltase deficiency with minimal starch tolerance

ORPHA: 306446

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

Orphanet Code

ORPHA:306446
congenital sucrase-isomaltase deficiency with minimal starch tolerance
OrphanetORPHA:306446
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
congenital sucrase-isomaltase deficiency with minimal starch tolerance | OrphanDrug