congenital sucrase-isomaltase deficiency with starch intolerance
ORPHA: 3064361 Treatment Available
Overview
human disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Sacrosidase Orphan | Oral solution | FDA Approved | 2 | — |
Classification & Codes
Orphanet Code
ORPHA:306436congenital sucrase-isomaltase deficiency with starch intolerance
| Orphanet | ORPHA:306436 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO