constitutional dyserythropoietic anemia
ORPHA: 2938301 Treatment Available
Overview
human disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| luspatercept Orphan Cold Chain | subcutaneous injection, 25 mg/vial, 75 mg/vial powder for solution | FDA Approved, EMA Approved | 8 | 10d |
Classification & Codes
Orphanet Code
ORPHA:293830constitutional dyserythropoietic anemia
| Orphanet | ORPHA:293830 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO