cystathioninuria

MeSH: C535408ORPHA: 212

Overview

amino acid metabolic disorder characterized by elevated plasma and urinary cystathionine levels that has material basis in homozygous or compound heterozygous mutation in the CTH gene on chromosome 1p31

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with cystathioninuria, sourced from HPO and Orphanet clinical annotations.

CystathioninuriaIntellectual disabilitySeizureCystathioninemiaNephrolithiasisTremorTalipes equinovarusAbnormal pinna morphology

Classification & Codes

MeSH Code

C535408

Orphanet Code

ORPHA:212
cystathioninuria
MeSHC535408
OrphanetORPHA:212
Treatments0 drug(s)
Symptoms on record8 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO