demyelinating hereditary motor and sensory neuropathy
ORPHA: 4761161 Treatment Available
Overview
human disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Eteplirsen Orphan Cold Chain | IV infusion | FDA Approved | 1 | — |
Classification & Codes
Orphanet Code
ORPHA:476116demyelinating hereditary motor and sensory neuropathy
| Orphanet | ORPHA:476116 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO