distal myopathy with vocal cord weakness

ORPHA: 600

Overview

Distal myopathy with vocal cord and pharyngeal weakness is an adult-onset, autosomal dominant muscular disease which is characterized by muscle weakness in the feet and hands, combined with vocal or swallowing dysfunction

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with distal myopathy with vocal cord weakness, sourced from HPO and Orphanet clinical annotations.

DysarthriaBulbar palsyHyperreflexiaAbnormal calf musculature morphologyVocal cord paresisHoarse voiceHypernasal speechWeak voiceDysphagiaUnsteady gaitDistal muscle weaknessRespiratory insufficiency due to muscle weaknessAspirationEMG abnormalityExercise-induced myalgiaRimmed vacuolesImperfect vocal cord adductionAmyotrophic lateral sclerosisMildly elevated creatine kinaseBowing of the vocal cordsAnkle weaknessAbnormal morphology of musculature of pharynxShoulder girdle muscle weaknessDistal upper limb amyotrophyAbnormality of the extraocular musclesDementiaDecreased nerve conduction velocityDistal sensory impairmentGait disturbance

Classification & Codes

Orphanet Code

ORPHA:600
distal myopathy with vocal cord weakness
OrphanetORPHA:600
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
distal myopathy with vocal cord weakness | OrphanDrug