familial idiopathic steroid-resistant nephrotic syndrome

ORPHA: 656

Overview

Familial idiopathic steroid-resistant nephrotic syndrome is characterized by a nephrotic syndrome with often early onset

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with familial idiopathic steroid-resistant nephrotic syndrome, sourced from HPO and Orphanet clinical annotations.

ProteinuriaEdemaFocal segmental glomerulosclerosisStage 5 chronic kidney diseaseChronic kidney diseasePeriorbital edemaIrritabilityFeverDiffuse mesangial sclerosisAbdominal painHeadacheHypoalbuminemiaRespiratory tract infectionMinimal change glomerulonephritisFoamy urineAbnormality of the nervous systemPeritonitis

Classification & Codes

Orphanet Code

ORPHA:656
familial idiopathic steroid-resistant nephrotic syndrome
OrphanetORPHA:656
Treatments0 drug(s)
Symptoms on record17 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO