fatal multiple mitochondrial dysfunctions syndrome

MeSH: C565304ORPHA: 289573

Overview

mitochondrial metabolism disease that is characterized by variants in genes involved in mitochondrial energy production, resulting in impairment of energy production at more than one stage of energy metabolism

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

C565304

Orphanet Code

ORPHA:289573
fatal multiple mitochondrial dysfunctions syndrome
MeSHC565304
OrphanetORPHA:289573
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO