galactosemia

MeSH: D005693ORPHA: 352

Overview

carbohydrate metabolic disorder that involves a defect in galactose metabolism resulting in toxic levels of galactose 1-phosphate in various tissues

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

D005693

Orphanet Code

ORPHA:352
galactosemia
MeSHD005693
OrphanetORPHA:352
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
galactosemia | OrphanDrug