Gaucher disease-ophthalmoplegia-cardiovascular calcification syndrome

ORPHA: 2072

Overview

Gaucher disease - ophthalmoplegia - cardiovascular calcification is a variant of Gaucher disease, also known as a Gaucher-like disease that is characterized by cardiac involvement

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Gaucher disease-ophthalmoplegia-cardiovascular calcification syndrome, sourced from HPO and Orphanet clinical annotations.

HepatosplenomegalyThrombocytopeniaDecreased beta-glucocerebrosidase levelAortic valve calcificationMitral valve calcificationCalcification of the aortaCorneal opacityElevated circulating glucosylsphingosine concentrationHydrocephalusSensorineural hearing impairmentStrabismusOphthalmoplegiaOculomotor apraxiaIntellectual disabilitySeizureSpastic paraplegiaHyporeflexiaGait disturbanceHyperreflexiaGrowth delayAortic valve stenosisMitral regurgitationVentricular hypertrophyMitral stenosisSplenomegalyPes cavusHallux valgusPancytopeniaAnemiaHypoplasia of the corpus callosumVentriculomegalyPulmonary fibrosisHeadacheSpontaneous, recurrent epistaxisAttention deficit hyperactivity disorderAzoospermiaBrachycephalyPtosisAbnormal saccadic eye movementsSupranuclear gaze palsyPectus excavatumHyperextensible skinCholelithiasisMotor delayHypertoniaEsophageal varixLimb ataxiaPulmonary arterial hypertensionScoliosisThoracolumbar kyphosisAbnormal pulmonary interstitial morphologyBacterial endocarditisOpsoclonusFeeding difficultiesAbnormal temper tantrumsEcchymosisSkin ulcer

Classification & Codes

Orphanet Code

ORPHA:2072
Gaucher disease-ophthalmoplegia-cardiovascular calcification syndrome
OrphanetORPHA:2072
Treatments0 drug(s)
Symptoms on record57 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO