genetic cardiac disease
ORPHA: 980541 Treatment Available
Overview
rare genetic heart disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Ataluren Orphan | Powder for oral suspension | EMA Approved | 5 | 21d |
Classification & Codes
Orphanet Code
ORPHA:98054genetic cardiac disease
| Orphanet | ORPHA:98054 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO