Glucocorticoid deficiency 1

ORPHA: 361

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Glucocorticoid deficiency 1, sourced from HPO and Orphanet clinical annotations.

Precocious pubertyDecreased circulating aldosterone concentrationTesticular adrenal rest tumorRecurrent urinary tract infectionsAzoospermiaCongenital hypothyroidismIntellectual disabilityHypoglycemic comaHypertrophic cardiomyopathyTetraplegiaLeydig cell neoplasiaAdrenal insufficiencyDecreased circulating cortisol levelFailure to thriveHypotensionGeneralized hyperpigmentationAbnormal circulating adrenocorticotropin concentrationKetotic hypoglycemiaImpaired cortisol response to insulin stimulation testDecreased circulating dehydroepiandrosterone concentrationRenal salt wastingWeight lossVomitingDiarrheaConstipationAnorexiaHyperkalemiaHypoglycemic seizuresEpisodic abdominal painRecurrent infectionsHyponatremiaChronic fatigueHypernatriuriaCryptorchidismTall stature

Classification & Codes

Orphanet Code

ORPHA:361
Glucocorticoid deficiency 1
OrphanetORPHA:361
Treatments0 drug(s)
Symptoms on record35 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO